The Pompe Registry: tracking Pompe disease symptoms in a broad patient population
نویسندگان
چکیده
Address: 1Congenital Heart Center University of Florida, College of Medicine, Gainesville, FL, USA, 2Duke University Medical Center, Durham, NC, USA, 3Department of Medical Genetics, University of Ferrara, Ferrara, Italy, 4Department of Neurology, University of Munich, Munich, Germany, 5Erasmus Medical Center, Sophia,, Rotterdam, Netherlands and 6Genzyme Corporation, Cambridge, MA, USA * Corresponding author
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